1:00 - 1:05 | Welcome and Introductions
1:05 - 1:15 | Need for improving outcomes in MMA and PA and new approaches entering clinical trials
1:15 - 1:30 | Pharmacology and preclinical data on oral small molecule HST5040
1:30 - 1:45 | HERO phase 2 clinical study design
1:45 - 2:00 | Moderated Questions and Answers
Gregory Enns, MD
Professor of Pediatrics, Stanford University
Kimberly Chapman, MD, PhD
Geneticist and Metabolist, Children’s National Hospital
Brian Wamhoff, PhD
Co-Founder and Chief Operating Officer, HemoShear Therapeutics
Gerald Cox, MD, PhD
Chief Medical Officer, HemoShear Therapeutics
Molecular Genetics and Metabolism has published in vitro pharmacology data supporting the oral small molecule HST5040 as a potential novel treatment for MMA and PA.
HemoShear Therapeutics, Inc.
501 Locust Avenue
Suite 301
Charlottesville, Virginia 22902